Exa-cel, a new CRISPR-based treatment, modifies the genes of the patient's stem cells to induce them to produce fetal hemoglobin.
Sickle cell anemia
Sepsis, a microbial infection that’s overwhelming, remains one of the most significant sources of morbidity and mortality. In the U.S., “black individuals” have both a greater risk of hospitalization and death than their “white” counterparts. While exposure and susceptibility may have roots in socioeconomic disparity, a new paper suggests that genetics may influence outcomes more than disparate care.
As if our policies for treatment of pain patients aren't horrific enough? If you happen to be black or Hispanic and suffer from Sickle Cell Disease, life is far worse. Do patients with a known, easily-diagnosed disease get a break with pain relief? No, it's quite the opposite. Disgraceful.
To underscore how important the battle for its eradication still is, misperceptions are clarified and key aspects of the inherited illness are addressed here.
The actor and musician knows how to convey a message that effects medical change, helped in part by his visit top be with sick kids at Children's Hospital Los Angeles. Now, let's see if Hollywood follows suit.
ACSH's Director of Medicine, Dr. Jamie Wells, traveled to Washington, DC to tape at Al Jazeera for a live television program. It engaged a global discussion on sickle cell anemia, its perils and the advances in gene therapy that are showing great promise for this genetic disease.